SNP-based Microdeletion and Aneuploidy RegisTry (SMART) Read more about SNP-based Microdeletion and Aneuploidy RegisTry (SMART)
Transthyretin Amyloidosis Outcome Survey (THAOS) Read more about Transthyretin Amyloidosis Outcome Survey (THAOS)
VTS-270 to Treat Niemann-Pick Type C1 (NPC1) Disease Read more about VTS-270 to Treat Niemann-Pick Type C1 (NPC1) Disease
Prompt Panretinal Photocoagulation Versus Ranibizumab+Deferred Panretinal Photocoagulation for Proliferative Diabetic Retinopathy Read more about Prompt Panretinal Photocoagulation Versus Ranibizumab+Deferred Panretinal Photocoagulation for Proliferative Diabetic Retinopathy
Cerebrotendinous Xanthomatosis (CTX) Prevalence Study Read more about Cerebrotendinous Xanthomatosis (CTX) Prevalence Study
Study to Evaluate Safety and Efficacy of Dapagliflozin in Patients With Type 2 Diabetes Mellitus Aged 10-24 Years Read more about Study to Evaluate Safety and Efficacy of Dapagliflozin in Patients With Type 2 Diabetes Mellitus Aged 10-24 Years
A Phase 3 Study to Evaluate the Safety of Sotagliflozin in Patients With Type 1 Diabetes Who Have Inadequate Glycemic Control With Insulin Therapy Alone Read more about A Phase 3 Study to Evaluate the Safety of Sotagliflozin in Patients With Type 1 Diabetes Who Have Inadequate Glycemic Control With Insulin Therapy Alone
A Study of SIMPONI® to Arrest Beta-cell Loss in Type 1 Diabetes Read more about A Study of SIMPONI® to Arrest Beta-cell Loss in Type 1 Diabetes
A Study Comparing Cardiovascular Effects of Ticagrelor Versus Placebo in Patients With Type 2 Diabetes Mellitus Read more about A Study Comparing Cardiovascular Effects of Ticagrelor Versus Placebo in Patients With Type 2 Diabetes Mellitus
ENDEAVOUR: Phase 3 Multicenter Study of Revusiran (ALN-TTRSC) in Patients With Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC) Read more about ENDEAVOUR: Phase 3 Multicenter Study of Revusiran (ALN-TTRSC) in Patients With Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC)